TY - JOUR
KW - Humans
KW - Male
KW - *Muscular Dystrophy, Duchenne/epidemiology/therapy
KW - Retrospective Studies
KW - Longitudinal Studies
KW - Adrenal Cortex Hormones
KW - *Cardiomyopathies/complications
KW - United Kingdom/epidemiology
KW - Duchenne muscular dystrophy
KW - Economic models
KW - Electronic Health Records
KW - statistical models
KW - fees from Duchenne UK. Michela Guglieri has received research funding from
KW - Sarepta, PTC, Muscular Dystrophy UK, NIH and H2020
KW - is (or has been) chief
KW - investigator/principal investigator for clinical trials of Pfizer, Italfarmaco,
KW - Santhera, Roche, ReveraGen, Dynacure, Dyne
KW - is a member of Advisory boards for
KW - Pfizer, NS Pharma, Dyne (honoraria through Newcastle University)
KW - and has
KW - received speaker honoraria from Sarepta, Italfarmaco, Novartis and Roche.
AU - J. Broomfield
AU - K. Abrams
AU - N. Latimer
AU - M. Guglieri
AU - M. Rutherford
AU - M. Crowther
AD - Department of Population Health Sciences, University of Leicester, Leicester, UK.
Department of Statistics, University of Warwick, Coventry, UK.
Centre for Health Economics, University of York, York, UK.
School of Health and Related Research (ScHARR), University of Sheffield, Sheffield, UK.
John Walton Muscular Dystrophy Research Centre, Newcastle University and Newcastle Hospitals NHS, Newcastle, UK.
Red Door Analytics, Stockholm, Sweden.
AN - 37957895
BT - Brain Behav
C2 - PMC10726817
DO - 10.1002/brb3.3331
DP - NLM
ET - 2023/11/14
LA - eng
M1 - 12
N1 - 2162-3279
Broomfield, Jonathan
Orcid: 0000-0003-1846-2150
Abrams, Keith
Latimer, Nick
Guglieri, Michela
Rutherford, Mark
Crowther, Michael
NIHR300984/National Institute for Health and Care Research/
Journal Article
United States
Brain Behav. 2023 Dec;13(12):e3331. doi: 10.1002/brb3.3331. Epub 2023 Nov 13.
PY - 2023
EP - e3331
T2 - Brain Behav
TI - Natural history of Duchenne muscular dystrophy in the United Kingdom: A descriptive study using the Clinical Practice Research Datalink
VL - 13
ER -